Though in our hearts we desire to be free from DBA, we have learned patience, love, trust, perseverance, compassion, courage, and to cry.
Tag Archives: The Feinstein Institute for Medical Research
DBA Gene Therapy Research Funded by DBAF & DBAC
The Diamond Blackfan Anemia Foundation is proud to partner with DBA Canada to fund a novel gene therapy research proposal from Dr. Johnson Liu, MD at The Feinstein Institute for Medical Research. The $48,210 project is titled, “Repairing Dominant Negative Mutation of RPS19 Gene by Spliceosome-Mediated RNA Trans-Splicing.” This approach takes advantage of the fact that human genes are made Continue Reading »