Skip to Content

for patients…for families…for research

Tag Archives: The Feinstein Institute for Medical Research

DBA Gene Therapy Research Funded by DBAF & DBAC

The Diamond Blackfan Anemia Foundation is proud to partner with DBA Canada to fund a novel gene therapy research proposal from Dr. Johnson Liu, MD at The Feinstein Institute for Medical Research. The $48,210 project is titled, “Repairing Dominant Negative Mutation of RPS19 Gene by Spliceosome-Mediated RNA Trans-Splicing.” This approach takes advantage of the fact that human genes are made  Continue Reading »