Dr. Harvey Lodish of the Whitehead Institute published new findings identifying a protein that is the target of prednisone or prednisolone, the drugs that are used to increase red blood cell production in some patients with Diamond Blackfan Anemia. The discovery could spur development of drugs capable of increasing this protein’s production without causing the severe side effects associated with glucocorticoids. Click the title to read the full article, Scientists Identify Potential Drug Target for Treatment-Resistant Anemias.
It has been seven years since DBA became part of our vocabulary. Our son’s diagnosis brought confusion, apprehension and despair. The discovery of DBAF is a stroke of serendipity. While even more tears were shed, these are now mingled with knowledge, understanding and, more significantly, hope. It will be through research that our son will be able to secure a brighter future.